Empowering families with knowledge, clarity, and confidence to navigate clinical trials and emerging therapies for Rett syndrome. Whether you’re just starting to explore clinical research or ready to take the next step, Rett Forward is your guide to understanding the process, evaluating opportunities, and moving forward with hope.
Introducing IRSF's newest learning platform
Rett Forward offers a clear, accessible path for families seeking to better understand the process of clinical trials. Designed with input directly from the Rett community, the three thoughtfully designed modules in this self-paced educational course break down key topics like trial design, participant experience, and emerging treatments—including cutting-edge approaches like gene therapy. Rett Forward bridges the gap between complex science and everyday decision-making, helping families feel prepared for conversations about research and care.
Discover the Value of Rett Forward
The clinical research journey can feel overwhelming—but Rett Forward was designed to make it clear, approachable, and empowering for families. Here’s what makes it a valuable resource:
Learn from the Experts
Hear directly from world-renowned Rett researchers and clinicians.
High-Quality, Engaging Lessons
Enjoy concise, easy-to-follow videos designed for busy families.
Up-to-Date Information
Access the latest on emerging therapies, clinical trials, and more.
Make Informed Decisions
Learn what to ask, what to consider, and how to move forward.
What’s covered in the course?
Rett Forward is built to simplify complex topics and provide you with a clear understanding of how clinical trials work—what they involve, how they’re developed, and what to expect if you choose to participate. Across three focused modules, the course walks through the science behind Rett syndrome, potential treatments like gene therapy, trial design, and real-world considerations—giving you the knowledge to explore clinical research on your own terms.
Gene Therapy: Foundations, Design, and Administration
- 10 Lessons
- 1.5hr
Explore the science behind genetic treatments and how they are being developed to treat Rett syndrome. This module covers everything from DNA and RNA basics to delivery methods, dosing, immune response, and long-term impact.
- Get grounded in the biology
- Understand how gene therapy works
- Learn what’s inside the treatment and how it’s delivered
The Clinical Trial Process: From Research to Approval
- 10 Lessons
- 1.5hr
Follow the full path of a clinical trial—from preclinical research to FDA approval. This module explains how trials are designed, who can participate, what risks are involved, and how new treatments move from experimental to approved.
- See how trials are designed and phased
- Find out who qualifies and what participation involves
- Learn how success is measured and treatments get approved
Participation Considerations and Looking to the Future
- 10 Lessons
- 1.5hr
Look beyond the basics to understand what participation really means and where Rett research is headed next. This module covers real-world factors like time, travel, and expectations—plus a look at future therapy options and how your involvement can help drive progress.
- Get clear on the potential time, travel, and commitment involved
- Explore future treatment possibilities still in development, like gene and RNA editing
- Discover how participation shapes the future of Rett research
Our Expert Collaborators
Meet the clinicians, researchers, and thought leaders who helped shape Rett Forward—trusted voices in the Rett community who bring deep expertise and real-world insight to every lesson.
Our Sponsors
This programming was made possible through the generous support of the following:
Questions about Rett Forward? We want to hear from you!
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Rett Research & Clinical Pipeline
Stay informed about the latest developments in Rett syndrome research and the clinical pipeline. IRSF is your trusted partner in navigating the complexities of therapeutic development and clinical trials.